February 13, 2020

Plenty of Rare Diseases, But Limited Options for Treatment

Image of lab tech's hand dropping liquid into test tubes

The National Institutes of Health defines a rare disease as “a condition that affects fewer than 200,000 people.” It also estimates that 25 to 30 million people in the United States is living with one of the ~7,000 known rare diseases, yet treatments are only available for about 5% of those ~7,000!

As if that weren’t enough, other challenges persist for these patients, including access issues born of high prices and licensing delays. Lest anyone think such issues get easier ex-U.S., think again; they’re common across the globe. — MM&M

To illustrate the barriers to treatment access, we’re sharing this insightful infographic created by the staff at MM&M, which looks at the stats around patient need, drug availability, variability of access and costs associated with rare disease treatments.

We hope you’ll take a few minutes to check it out and learn more about this important topic!

Image of MM&M infographic